Could CRISPR cure rare diseases before birth? Scientists are getting closer
Dr. Kiran Musunuru is the co-director of the Penn Medicine/CHOP Orphan Disease Center. CNBC One of the keys to curing a rare disease is treating…
Tag: BridgeBio Pharma Inc
New bipartisan bill aims to speed up clinical trials for rare disease treatments
The U.S. Capitol in Washington, D.C., on Aug. 5, 2026. Aaron Schwartz | Bloomberg | Getty Images One week after the Food and Drug Administration…